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全部话题 - 话题: biomarin
1 (共1页)
h*****g
发帖数: 42
1
【 以下文字转载自 SanFrancisco 讨论区 】
发信人: hooking (hooking), 信区: SanFrancisco
标 题: 黏多糖症紧急求助,有在BioMarin 公司的吗?
发信站: BBS 未名空间站 (Thu Sep 29 13:09:22 2011, 美东)
国内朋友的小孩得了黏多糖症(4型),现在世界上还没有可用的药。BioMarin公司已经
开发了针对黏多糖6型的药,现在针对黏多糖4型的药正在进行三期临床试验。这边有在
BioMarin公司工作的兄弟姐妹吗?能否帮忙打听下公司内招募病人都如何操作的?他们
的临床试验几乎是唯一的希望了。眼睁睁看着孩子一天天严重下去,心如刀割啊!
先行谢过各位好心人!
h*****g
发帖数: 42
2
【 以下文字转载自 SanFrancisco 讨论区 】
发信人: hooking (hooking), 信区: SanFrancisco
标 题: 黏多糖症紧急求助,有在BioMarin 公司的吗?
发信站: BBS 未名空间站 (Thu Sep 29 13:09:22 2011, 美东)
国内朋友的小孩得了黏多糖症(4型),现在世界上还没有可用的药。BioMarin公司已经
开发了针对黏多糖6型的药,现在针对黏多糖4型的药正在进行三期临床试验。这边有在
BioMarin公司工作的兄弟姐妹吗?能否帮忙打听下公司内招募病人都如何操作的?他们
的临床试验几乎是唯一的希望了。眼睁睁看着孩子一天天严重下去,心如刀割啊!
先行谢过各位好心人!
h*****g
发帖数: 42
3
【 以下文字转载自 SanFrancisco 讨论区 】
发信人: hooking (hooking), 信区: SanFrancisco
标 题: 黏多糖症紧急求助,有在BioMarin 公司的吗?
发信站: BBS 未名空间站 (Thu Sep 29 13:09:22 2011, 美东)
国内朋友的小孩得了黏多糖症(4型),现在世界上还没有可用的药。BioMarin公司已经
开发了针对黏多糖6型的药,现在针对黏多糖4型的药正在进行三期临床试验。这边有在
BioMarin公司工作的兄弟姐妹吗?能否帮忙打听下公司内招募病人都如何操作的?他们
的临床试验几乎是唯一的希望了。眼睁睁看着孩子一天天严重下去,心如刀割啊!
先行谢过各位好心人!
c**********g
发帖数: 1607
4
【 以下文字转载自 Pharmaceutical 讨论区 】
发信人: wwwhu (fc), 信区: Pharmaceutical
标 题: Re: 黏多糖症紧急求助,有在BioMarin 公司的吗? (转载)
发信站: BBS 未名空间站 (Fri Nov 11 19:02:06 2011, 美东)
http://www.clinicaltrials.gov/ct2/results?term=Biomarin
every trial has its own contact, PI, try to contact them.
h*****g
发帖数: 42
5
国内朋友的小孩得了黏多糖症(4型),现在世界上还没有可用的药。BioMarin公司已经
开发了针对黏多糖6型的药,现在针对黏多糖4型的药正在进行三期临床试验。这边有在
BioMarin公司工作的兄弟姐妹吗?能否帮忙打听下公司内招募病人都如何操作的?他们
的临床试验几乎是唯一的希望了。眼睁睁看着孩子一天天严重下去,心如刀割啊!
先行谢过各位好心人!
w********o
发帖数: 1621
6
Didn't expect to see BioMarin on this board.
In order to be enrolled into their studies, you need go to participating
sites and asked to be evaluated. If you meet all the inclusion/exclusion
criteria, then you will be enrolled. To find out which sites are currently
screening patients, you can go to BioMarin's website or call them.
Before you get the kids to US to see those investigators, you better get a
clear idea what their screening criteria is by checking the inclusion/
exclusion details on ... 阅读全帖
b*******0
发帖数: 1695
7
You should call BioMarin, Clincal Dept. It is hard to find patients some
times.
b*******0
发帖数: 1695
8
You should call BioMarin, Clincal Dept. It is hard to find patients some
times.
w***u
发帖数: 17713
9
http://www.clinicaltrials.gov/ct2/results?term=Biomarin
every trial has its own contact, PI, try to contact them.
v**********m
发帖数: 5516
10
烟幕弹又来了,不知MM能拉到什么价位。
GlaxoSmithKline (GSK) And Biogen Idec (BIIB) Possible Candidates To Acquire
Human Genome Sciences (HGSI), Says Senior Analyst At Piper Jaffray; Read
More About This Prospect And Others In The Biotech Space In This Exclusive
Interview
November 21, 2011 - The Wall Street Transcript has just published
Biotechnology and Pharmaceuticals Report offering a timely review of the
Biotechnology sector. This Special Report contains expert industry
commentary through in-depth interviews w... 阅读全帖
c*******u
发帖数: 12899
11
来自主题: NextGeneration版 - [合集] [bssd]我的孩子,我的经历
☆─────────────────────────────────────☆
aprilxu (妞妞是个乖宝宝) 于 (Fri Mar 30 00:33:44 2012, 美东) 提到:
我已经很久很久不发帖了,自从我女儿确诊以后,我就再没有心思在网上发帖和回帖了
。这几天看了一些关于残疾孩子和流产的帖子,我忍不住想说几句我自己的经历,也算
是一种倾诉吧。
我女儿快三岁了,又漂亮又聪明,可是,她不会走路,而且永远也不会。她患有SMA (
Spinal Muscular Atrophy) 。这是一种genetic disorder,由于基因缺失身体无
法制造一种蛋白,严重影响她的运动神经元和所控制的肌肉,导致肌张力低下。SMA是
一种罕见病,发病率仅为万分之一,由于我和我老公都是携带者(我们都不知道,也没
有家族史),我们的孩子有四分之一的几率患病,我的女儿很不幸。
但是幸运的是,我的女儿不是最严重的情况。Type 1,也就是最严重的情况,孩子一般
不会活过两岁。我女儿属于type 2,医生没说能活多久,只是告诉我们,最终依靠仪器
,她也许能活到成年,能上college,但是... 阅读全帖
d******i
发帖数: 1379
12
来自主题: NextGeneration版 - [bssd]我的孩子,我的经历
您好,能提供一下具体的途径么,我认识国内患SMA的孩子,很想知道如何帮助她们

。我前些日子帮一个国内的小孩联系到Biomarin 的一个朋友,然后那个朋友帮他们联
系到了去台湾Biomarin 的 clinical trial site做黏多糖症(4型)的治疗。所以SMA也
许以后会有办法治的,小宝宝说不定有站起来的一天。
y*****l
发帖数: 5997
13
Stocks to Watch at JPMorgan Healthcare Conference
By David Miller Jan 07, 2011 3:00 pm
Next week investors will congregate in California to discuss the future of
the biotech industry. Companies to watch include Exelixis, Medivation, and
Dendreon.
It’s the time of year for the JPMorgan (JPM) Healthcare Conference. The
conference, which runs Monday through Thursday next week in San Francisco,
is the surest place to see everyone in biotech each year. The size of the
crowd at the conference, held at... 阅读全帖
y*****l
发帖数: 5997
14
Stocks to Watch at JPMorgan Healthcare Conference
By David Miller Jan 07, 2011 3:00 pm
Next week investors will congregate in California to discuss the future of
the biotech industry. Companies to watch include Exelixis, Medivation, and
Dendreon.
It’s the time of year for the JPMorgan (JPM) Healthcare Conference. The
conference, which runs Monday through Thursday next week in San Francisco,
is the surest place to see everyone in biotech each year. The size of the
crowd at the conference, held at... 阅读全帖
q********g
发帖数: 10694
15
来自主题: _pennystock版 - 又一篇pump文章,关于SRPT
观点很象这里Jenny12以前说的。从中也学习到一些分析医药股的方法。例文欣赏。
http://seekingalpha.com/article/895051-sarepta-therapeutics-loo
Sarepta Therapeutics Looks Highly Undervalued
September 28, 2012 | 37 commentsby: Sean Anderson | about: SRPT
R.S. Analytics wrote up the long case for Sarepta Therapeutics (SRPT)
earlier this month here. I agree with that thesis, and won't bore everyone
by repeating it here since R.S. did such a great job telling it already.
There are, however, a few points that I'd like to expand on.
In ... 阅读全帖
u**l
发帖数: 1043
16
来自主题: NextGeneration版 - [bssd]我的孩子,我的经历
可爱的宝宝,伟大的爸爸妈妈。我知道有些医药公司是专门做这种orphan disease的。
我前些日子就帮一个国内的小孩联系到Biomarin 的台湾clinical trial site做黏多糖
症(4型)的治疗。所以这个病也许以后会有办法治的,小宝宝说不定有站起来的一天。
祝福小宝宝!!!
e*****7
发帖数: 31
17
BMY-IMCL deal gets done and may be in a higher price around 65-70. IMCL
jumped 20 to 65 from yesterday's close of 45.
Here are the list of comapnies on speculation list of future dating game:
Amylin/Eli Lilly (Byetta); OSI/Genentech (Tarceva); Biogen/Genentech (
Rituxan); Genzyme/BioMarin (Aldurazyme); Vertex/JNJ (Telapravir); Human
Genome Sciences/Novartis & GSK (Albuferon & LymphoSTAT); Regeneron/Sanofi (
VEGF-TRAP) ; Onyx/Bayer (Nexavaar); Idenix/Novartis (various compounds) ;
Momenta/Novarti
w****r
发帖数: 245
18
大侠,分类都分好了,求神签
# Basic Materials, Agricultural Chemicals
AGU Agrium Inc.
AVD American Vanguard Corp.
CAGC China Agritech Inc.
CF CF Industries Holdings, Inc.
CGA China Green Agriculture, Inc.
CMP Compass Minerals International
COIN Converted Organics Inc.
IPI Intrepid Potash, Inc.
MON Monsanto Co.
MOS Mosaic Co.
NOEC New Oriental Energy & Chemical
POT Potas... 阅读全帖
a**********2
发帖数: 355
19
来自主题: Stock版 - 高盛每日晨报 3/25
微信公众平台 USOPTIONS
Americas : Market Intelligence – Morning Update
by Chris Hussey
Published March 25, 2014
Stocks in Asia were directionless Tuesday, trading in a relative news vacuum
as investors appear to be content to coast through the end of March. In
Europe this morning, however, equities are definitively higher although you
have to squint to find a reason for the reversal of yesterday's more bearish
tone. Overall, perhaps the daily trading gyrations of individual markets
are telling us l... 阅读全帖
d******8
发帖数: 1972
20
利好还是坏消息?
How Much? Gilead Pays $125M For an FDA Priority Review Voucher

By
Ed Silverman
David Gothard
For the first time since the FDA began a voucher program several years ago
to encourage development of drugs to treat neglected tropical diseases, a
drug maker has sold a voucher to another company. And the deal may help the
pharmaceutical industry ballpark the value of these vouchers.
In a brief statement, Knight Therapeutics says Gilead Sciences agGILD -1.32%
reed to pay $125 mi... 阅读全帖
d******5
发帖数: 4273
21
Earnings announcements on tap for tomorrow
Before the open (consensus views):
Sanofi (SNY -1%), Revenues of $39B.
Celgene (CELG -0.1%), EPS of $1.06 on revenues of $2.1B.
AmerisourceBergen (ABC -1.2%), EPS of $1.19 on revenues of $32.3B.
Teva Pharmaceutical Ind. (TEVA +1.1%), EPS of $1.25 on revenues of $4.8B.
Shire plc (SHPG -0.6%), EPS of $2.59 on revenues of $1.5B.
After the close:
Gilead Sciences (GILD -1.3%), EPS of $2.32 on revenues of $6.9B.
Biomarin Pharmaceuticals (BMRN -0.2%), loss per... 阅读全帖
t******t
发帖数: 21
22
来自主题: Stock版 - NASDAQ-100 强
NASDAQ上最大100家非金融公司。
https://www.cnbc.com/nasdaq-100/
Symbol Name
ATVI Activision Blizzard Inc
ADBE Adobe Inc.
AMD Advanced Micro Devices Inc
ALGN Align Technology Inc
ALXN Alexion Pharmaceuticals Inc
AMZN Amazon.com Inc
AMGN Amgen Inc
AAL American Airlines Group Inc
ADI Analog Devices Inc
AAPL Apple Inc
AMAT Applied Materials Inc
ASML ASML Holding NV
ADSK Autodesk Inc
ADP Automatic Data Processing Inc
AVGO Broadcom Inc
BIDU Baidu Inc
BIIB Bio... 阅读全帖
c**********g
发帖数: 1607
23
贵就贵在这里。医生有两种,一种是靠科研来钱;一种是靠门诊来钱。这些都是认识了
圈内人士才了解到的。
r*******e
发帖数: 60
24
来自主题: SanFrancisco版 - Biotech Career Fair in South San Francisco
http://www.ssfcareerevents.org/
Date: March 3, 2010
Time: 10am to 4pm
Location: South San Francisco Conference Center
Some of the companies attending:
Abbott
Affymetrix
Baxter
BioMarin
Boston Scientific
Catholic Healthcare West
Cepheid
FibroGen
Fluidigm
Genomic Health
Geron
Gilead
Impax Laboratories
Intuitive Surgical
MediImmune
Medivation
Live Leaf
Nektar
Novartis - Emeryville
Novartis - San Carlos
Pharmatech
ProGenTech
StemCells, Inc.
SuperGen
United Biosource
veracyte
XDx
Zeltiq Aesthetics
Go
h*****g
发帖数: 42
25
自己先顶一下。
u**l
发帖数: 1043
26
I have a friend there and I will help you ask her.
h*****g
发帖数: 42
27
太好了,谢谢谢谢!
j*****u
发帖数: 446
28
http://clinicaltrials.gov/
find all clinical trails from here. hope it helps.
h*****g
发帖数: 42
29
Judyzhu,谢谢你!
h*****g
发帖数: 42
30
Thanks for your reminder. I went through the inclusion/exclusion criteria on
their trial website, it's a randomized and double-blind study.
M*****R
发帖数: 650
31
Just asked. They are doing clinical trial on this, but probably not in China
. Not sure how this can work out.
Anyway, check your mitbbs mail for contact info.
Q***N
发帖数: 2972
32
来自主题: SanFrancisco版 - 码工的生活好像不如药工
没什么好辩论的。 NJ/PA/SD是有不少美国的药厂, 但是要说SF不敢说有药厂,我只能
说无知者无畏。
美国的几个大制药公司起的头, MBA出身的CEO都在想着怎么开源节流。(尤其是美国
公司)都在缩减自己的研发,喜欢买其它公司的半成品来降低成本,这是目前的发展趋
势。 当前也就为数不多的家大公司(包括瑞士的RACHE和NORVATIS,以及欧洲一家专长
糖尿病)还能保持不缩减对自身的科研队伍。所以现在大公司的职位越来越少, 公司
合并后的裁人也越来越多。
带来的正面影响是小公司越来越多, VC对生物/制药的STARTUP近几年投入惊人,你看
看SF的MISSION BAY和SSF的火热程度就知道了。生物/制药的STARTUP主要集中湾区和
BOSTON。 湾区占着VC资金的优势, BOSTON我不是很了解,但我知道那里也是生物/制
药的STARTUP的集中地。 但NJ/PA,我对那里的STARTUP一无所知。
因为我自己不是这个圈子里的人,也许是我孤陋寡闻。 但我绝对敢说“ SF有药厂”。
更何况 Genentech/BioMarin/Bayer/Norvatis/Gilead都在... 阅读全帖
s********o
发帖数: 94
33
来自主题: Pharmaceutical版 - HR 面试
有些公司像biomarin是HR先prescreening下,然后才能给你转到相关HM那里才有HM的电
面。当然也有像genetech这样的HM直接联系你电面的,多数小公司也是HM直接电面。什
么情况都会有的。
h******s
发帖数: 3420
34
来自主题: Statistics版 - 统计硕士的出路
我是说director of biostatistics 20万,分四年。programmer 要少。每年50%
refresh. 难道大家以为我说的是20万/year?
我们公司是billion 了。去再小的拿的多一点,去再大的拿的少一点。
NDA 的确股票涨的快,几倍,几十倍的一般是有platform, 不停的file 新药,像
biomarin, Jazz pharma,Gilead 什么的.
这边一般在大公司攒点经验就去小公司。一般人喜欢赌merger, 2016 去medivation,
pharmacyclics, 去了几个月公司就被收购,一个个笑呵呵的等退休。
今年大家去cancer, 只要跟cancer 相关的股票一个个呼呼的涨,过两天一看被收购了。
搞这行不去小公司去哪儿?大公司都是卖现成的药,要biostatistician 干嘛?很多在
大公司干了十几年的没摸过NDA 的,好多公司只有registry.
而且大公司不是药过期就是被小公司打败,也就是cash 多靠买小公司过日子。不裁员
就不错了。今年allergen 股票都跌一半了,那硅谷的小公司才刚phase ... 阅读全帖
i***m
发帖数: 148
35
来自主题: Statistics版 - 统计硕士的出路
感觉你这个说的就片面了吧。
波士顿就被无视了?biotech最火的地方就是波士顿了吧。
而且你说的biomarin,gilead最近股票都很一般啊,别说几倍的涨了,gilead都跌了不
少。
去了几个月就被收购的,拿到手的股票也没多少吧?
大公司怎么就只卖现成的药了呢?这不是把几大巨头都给无视了吗?Pfizer,Merck,
Novartis,Lilly,BMS,Regeneron,Roche这些大公司每年都有新药出来啊,怎么就不
需要biostatistician了呢?
当然我同意你说的,富贵险中求,攒点经验还是去小公司更有得赚

了。
h******s
发帖数: 3420
36
来自主题: Statistics版 - 统计硕士的出路
我是说director of biostatistics 20万,分四年。programmer 要少。每年50%
refresh. 难道大家以为我说的是20万/year?
我们公司是billion 了。去再小的拿的多一点,去再大的拿的少一点。
NDA 的确股票涨的快,几倍,几十倍的一般是有platform, 不停的file 新药,像
biomarin, Jazz pharma,Gilead 什么的.
这边一般在大公司攒点经验就去小公司。一般人喜欢赌merger, 2016 去medivation,
pharmacyclics, 去了几个月公司就被收购,一个个笑呵呵的等退休。
今年大家去cancer, 只要跟cancer 相关的股票一个个呼呼的涨,过两天一看被收购了。
搞这行不去小公司去哪儿?大公司都是卖现成的药,要biostatistician 干嘛?很多在
大公司干了十几年的没摸过NDA 的,好多公司只有registry.
而且大公司不是药过期就是被小公司打败,也就是cash 多靠买小公司过日子。不裁员
就不错了。今年allergen 股票都跌一半了,那硅谷的小公司才刚phase ... 阅读全帖
i***m
发帖数: 148
37
来自主题: Statistics版 - 统计硕士的出路
感觉你这个说的就片面了吧。
波士顿就被无视了?biotech最火的地方就是波士顿了吧。
而且你说的biomarin,gilead最近股票都很一般啊,别说几倍的涨了,gilead都跌了不
少。
去了几个月就被收购的,拿到手的股票也没多少吧?
大公司怎么就只卖现成的药了呢?这不是把几大巨头都给无视了吗?Pfizer,Merck,
Novartis,Lilly,BMS,Regeneron,Roche这些大公司每年都有新药出来啊,怎么就不
需要biostatistician了呢?
当然我同意你说的,富贵险中求,攒点经验还是去小公司更有得赚

了。
X*****s
发帖数: 2767
38
By Michael Sedacca Jul 27, 2012 4:05 pm
Economics, earnings reports, and market events for the week ahead.
This next week will be extremely pivotal for the market. If Draghi can
follow up with his statements from Thursday and Friday, it is likely that
the market will continue its run higher. Draghi said on Friday that the ECB
was looking to start a new bond-buying program, cut rates, conduct another
special LTRO and give the ESM a banking license in the long term. Not only
is there the ECB meeti... 阅读全帖
w***y
发帖数: 2537
39
来自主题: _pennystock版 - Events and ER for week August 2-6 (转载)
【 以下文字转载自 Stock 讨论区 】
发信人: ll111 (Stealth), 信区: Stock
标 题: Events and ER for week August 2-6
发信站: BBS 未名空间站 (Sun Aug 1 22:47:17 2010, 美东)
Monday, Aug. 2
10 a.m.: ISM Manufacturing index on business activity in July, released by
the Institute for Supply Management.
10:15 a.m. Federal Reserve Chairman Ben Bernanke speaking on "challenges for
the economy and state governments."
4 p.m. Treasury Secretary Timothy Geithner speaking on the next steps for
financial reform.
Tuesday, Aug. 3
8:30 a.m.: P... 阅读全帖
v**********m
发帖数: 5516
40
来自主题: _pennystock版 - JP morgan healthcare conference Webcast
You guys now are able to listen to these web-castings now. Enjoy it!
http://jpmorgan.metameetings.com/webcasts/healthcare11/ondemand
individual Company Presentations
A
Abbott
Abiomed Inc. (available to Feb. 5)
Ablynx N.V.
Accretive Health Inc.
Accuray Inc.
Acorda Therapeutics, Inc. (available to Feb. 11)
Actelion Ltd
Aetna Inc. (available to Feb. 8)
Affymetrix Inc.
Agilent Technologies Inc.
Albany Molecular Research Inc.
Alere Inc (available to Feb. 11)
Alexion Pharmaceuticals, Inc. (not availab... 阅读全帖
v**********m
发帖数: 5516
41
来自主题: _pennystock版 - JP morgan healthcare conference Webcast
You guys now are able to listen to these web-castings now. Enjoy it!
http://jpmorgan.metameetings.com/webcasts/healthcare11/ondemand
individual Company Presentations
A
Abbott
Abiomed Inc. (available to Feb. 5)
Ablynx N.V.
Accretive Health Inc.
Accuray Inc.
Acorda Therapeutics, Inc. (available to Feb. 11)
Actelion Ltd
Aetna Inc. (available to Feb. 8)
Affymetrix Inc.
Agilent Technologies Inc.
Albany Molecular Research Inc.
Alere Inc (available to Feb. 11)
Alexion Pharmaceuticals, Inc. (not availab... 阅读全帖
f**********g
发帖数: 2252
42
来自主题: _pennystock版 - Biotech Calendar: Key Dates for February
http://www.thestreet.com/_yahoo/story/10989791/1/biotech-calend
By Adam Feuerstein 01/31/11 - 09:10 AM EST
ALIM, AEN, EXEL, PLX, GENZ, IDIX, AVNR
BOSTON, Mass. (TheStreet) -- A calendar of important, potentially stock-
moving biotech events for February:
More from Adam Feuerstein
NPS Pharma: Gattex Bowel Study SucceedsArena Pharma: Weight-Loss Drug
WoesBiotech Stock Mailbag: Orexigen TherapeuticsMarket Activity
AVANIR Pharmaceuticals| AVNR DOWNAlimera Sciences Inc.| ALIM DOWNProtalix
BioThera... 阅读全帖
f**********g
发帖数: 2252
43
来自主题: _pennystock版 - Biotech Calendar: Key Dates for February
http://www.thestreet.com/_yahoo/story/10989791/1/biotech-calend
By Adam Feuerstein 01/31/11 - 09:10 AM EST
ALIM, AEN, EXEL, PLX, GENZ, IDIX, AVNR
BOSTON, Mass. (TheStreet) -- A calendar of important, potentially stock-
moving biotech events for February:
More from Adam Feuerstein
NPS Pharma: Gattex Bowel Study SucceedsArena Pharma: Weight-Loss Drug
WoesBiotech Stock Mailbag: Orexigen TherapeuticsMarket Activity
AVANIR Pharmaceuticals| AVNR DOWNAlimera Sciences Inc.| ALIM DOWNProtalix
BioThera... 阅读全帖
d******8
发帖数: 1972
44
http://www.thestreet.com/story/11351242/1/10-biotech-stock-pred
BOSTON (TheStreet) -- Ten biotech predictions for 2012:
1. The Amgen(AMGN_) strategy of returning cash to shareholders in form of
share buybacks, Dutch tender offers and dividends is abandoned in favor of
ramped up acquisitions i.e. Gilead Sciences(GILD_) buying Pharmasset(VRUS_).
Large-cap biotech firms start acting like Big Pharma -- choosing to buy
growth instead of seeking it from internal drug development.
2. After much wrangli... 阅读全帖
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